Compositions and methods for targeting, editing or modifying human genes

Ryan T Gill (Inventor), Tanya Warnecke (Inventor), Roland Franz Baumgartner (Inventor)

Research output: Patent

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The present invention relates to engineered Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR) systems and corresponding guide RNAs that target specific nucleotide sequences at certain gene loci in the human genome. Also provided are methods of targeting, editing, and/or modifying of the human genes using the engineered CRISPR systems, and compositions and cells comprising the engineered CRISPR systems.

Original languageEnglish
IPCC12N 15/ 11 A I
Patent numberWO2021158918
Filing date05/02/2020
Country/TerritoryInternational Bureau of the World Intellectual Property Organization (WIPO)
Priority date05/02/2020
Priority numberUS202062970455P
Publication statusPublished - 12 Aug 2021


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